Amino acid formula with vitamins and minerals without methionine

PBAC's latest decision on Amino acid formula with vitamins and minerals without methionine: Recommended with restriction (2020). Considered for Dietary management of pyridoxine non-responsive homocystinuria (HCU).

Eligible population

Patients aged 3 years or over with pyridoxine non-responsive homocystinuria; the PBAC noted that prescribing is usually by specialists and nutritionists, and due to the formulation, HCU Lophlex will likely be used in teenagers and adults.

Therapy area

Metabolic

Line of therapy

Not applicable

Evidence base

Cost-minimisation

Primary endpoint

Cost-minimisation

Comparator

HCU Express 15, HCU Cooler 20, HCU Lophlex LQ 20, XMET Maxamum

Economic model

Cost-minimisation

ICER note

Cost-minimisation analysis; no ICER calculated.

Submission history

• Nov 2015: Recommended · Restricted
• Jul 2020: Recommended with restriction · Restricted

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