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PegfilgrastimPelgraz

Recommended OncologyAuthority RequiredNot applicable line 💬 consumer voice

Chemotherapy-induced neutropenia in patients receiving chemotherapy with intention of achieving cure or substantial remission, who are at greater than 20% risk of developing febrile neutropenia or at substantial risk of prolonged severe neutropenia for ≥7 days.

11
Submissions
4 resub
2006–20
On the record
$15k–45k
ICER range
5 sourced ICERs · 2006–2018
Cost-min
Cost basis

Decisions on record

13 decisions
  • Meeting Mar 2020 Recommended Chemotherapy- induced neutropenia
  • Meeting Nov 2019 Recommended Chemotherapy-induced neutropenia
  • Meeting Nov 2018 Recommended Chemotherapy-induced neutropenia no PSD
  • Meeting Jul 2018 Deferred Chemotherapy-induced neutropenia
  • Meeting Mar 2018 Recommended Prophylaxis of chemotherapy induced neutropenia
  • Meeting Jul 2017 Deferred Prophylaxis of chemotherapy induced neutropenia
  • Meeting Mar 2011 Recommended Bone marrow cell stimulator no PSD
  • Meeting Jul 2009 Recommended Neutropenia no PSD
5 earlier decisions
  • Nov 2008 Recommended Immunostimulant
  • Mar 2008 Not recommended Prevention of neutropenia.
  • Nov 2007 Recommended Neutropenia no PSD
  • Jul 2007 Recommended Prevention of neutropenia
  • Sep 2002 Recommended Stimulates production of white blood cells. no PSD

Access path

11 submissions · public record
  1. TGA registered · Pelgraz

    TGA label narrower than the PBS population

  2. Nov 2006
    Recommended

    Listing: Private hospital authority required → Restricted

  3. Nov 2006
    Recommended · restricted

    Listing: Private hospital authority required → Restricted

  4. Jul 2007
    Recommended

    Comparator changed: placebo plus secondary prophylactic use of pegfilgrastim → no…

  5. Jul 2007
    Recommended · restricted

    Comparator changed: placebo plus secondary prophylactic use of pegfilgrastim → no…

  6. Mar 2008
    Not recommended

    Uncertain clinical benefit (no survival benefit demonstrated as chemotherapy dose intensity was maintained in both…

  7. ↻ resubmitted
    Nov 2008
    Recommended · restricted

    Comparator changed: No G-CSF (advanced breast cancer); pegfilgrastim secondary…

  8. Jul 2017
    Deferred

    Comparator changed: filgrastim → secondary prophylaxis

  9. Mar 2018
    Recommended · restricted

    Comparator changed: secondary prophylaxis → no treatment (placebo) for primary…

  10. Jul 2018
    Recommended · restricted

    Comparator changed: no treatment (placebo) for primary prophylaxis; secondary prophylaxis…

  11. Nov 2019
    Recommended · restricted

    Listing: Authority Required → Restricted

  12. Mar 2020
    Recommended · restricted

    Comparator changed: Neulasta (pegfilgrastim reference brand) → Neulasta

  13. PBS listing · Authority Required
RecommendedDeferredNot recommended

From the public summary

Verbatim · PSD text · may span indications
PBAC outcome
6.1 The PBAC recommended the listing of the biosimilar brand of pegfilgrastim, Pelgraz, on the basis that it should only be available under special arrangements under Section 100 (Highly Specialised Drugs program) for all indications for which the reference brand (Neulasta) is currently PBS-listed.PSD · Mar 2020
6.2 The PBAC recommended listing Pelgraz on a cost-minimisation basis to the Neulasta brand of pegfilgrastim, and noted that this would result in no net cost to the Government because the listing of Pelgraz is not expected to grow the market. 5PSD · Mar 2020
Economic analysis
5.12 The minor submission presented a cost-minimisation analysis of Pelgraz compared with Neulasta. The equi-effective doses were estimated as 6 mg of Pelgraz is equal to 6 mg of Neulasta for the same frequency and duration of therapy.PSD · Mar 2020
5.13 The Sponsor noted the price reductions applied to pegfilgrastim in 2017 following listing of the Ristempa brand, and in 2018 following the broadening of the restriction as recommended by the PBAC in March 2018 with a price reduction to ensure a cost- effective listing in the expanded population. The minor submission requested an ex- manufacturer price for Pelgraz equivalent to that of Neulasta at the time of listing.PSD · Mar 2020
Clinical claim
5.9 The submission claimed non-inferior comparative effectiveness and non-inferior comparative safety of Pelgraz compared with Neulasta. The TGA Delegate was satisfied that the data for Pelgraz demonstrated an equivalent level of efficacy and safety for the desired indication as the comparator drug. 4PSD · Mar 2020
5.10 The PBAC considered that the claim of non-inferior comparative effectiveness was reasonably supported by the data.PSD · Mar 2020
Consumer comments
6.2 The PBAC noted and welcomed the input from health care professionals (1) and organisations (1) via the Consumer Comments facility on the PBS website. The comments indicated that treatment with pegfilgrastim as primary prophylaxis for febrile neutropenia could improve outcomes by enabling more aggressive treatment.PSD · Jul 2017
6.3 The PBAC also noted the advice received from the Medical Oncology Group of Australia (MOGA), which indicated that there were additional patient groups, such as those undergoing dose dense chemotherapy with anthracycline and cyclophosphamide, or treatment with paclitaxel, who would also benefit from this therapy.PSD · Jul 2017

Cost-effectiveness

5 sourced ICERs · 2006–2018

Cost-minimisation analysis; no ICER calculated by design. Submission assumed Pelgraz would be listed at same price as Neulasta with no net cost to Government.

The PBAC recommended listing Pelgraz on a cost-minimisation basis to the Neulasta brand of pegfilgrastim, and noted that this would result in no net cost to the Government because the listing of Pelgraz is not expected to grow the market. PBAC · 2020
ICER uncertain ×2Economic model disputed ×2Surrogate endpoint ×3Cost-effectiveness accepted ×6

Decision context

PopulationCancer patients receiving chemotherapy with intention of achieving cure or substantial remission who are at greater than 20% risk of developing febrile neutropenia or substantial risk of prolonged severe neutropenia for ≥7 days.

Submission history

11 entries
DecidedOutcomeComparatorICEREvidence
Mar 2020 Recommended · restricted Neulasta RCT · Other
Nov 2019 Recommended · restricted Neulasta (pegfilgrastim reference brand) RCT · Other
Jul 2018 Recommended · restricted Neulasta (pegfilgrastim reference brand) RCT · Duration of severe neutropenia (DSN) in Cycle 1
Mar 2018 Recommended · restricted no treatment (placebo) for primary prophylaxis; secondary prophylaxis for primary vs secondary comparison $15k–45k Cost-minimisation · Cost-minimisation
Jul 2017 Deferred secondary prophylaxis $15k–45k Meta-analysis · Febrile neutropenia rate
Nov 2008 Recommended · restricted filgrastim RCT · Febrile neutropenia prevention
Mar 2008 Not recommended No G-CSF (advanced breast cancer); pegfilgrastim secondary prophylaxis (early breast cancer) $15k–45k RCT · Febrile neutropenia
Jul 2007 Recommended no prophylaxis RCT · febrile neutropenia event avoided
Jul 2007 Recommended · restricted no prophylaxis RCT · FN
Nov 2006 Recommended placebo plus secondary prophylactic use of pegfilgrastim $30k RCT · Other
Nov 2006 Recommended · restricted placebo plus secondary prophylactic use of pegfilgrastim $30k RCT

Consumer voice

Jul 2017

Health care professionals and organisations indicated that pegfilgrastim as primary prophylaxis for febrile neutropenia could improve outcomes by enabling more aggressive treatment. The Medical Oncology Group of Australia advised that additional patient groups undergoing dose dense chemotherapy or paclitaxel treatment would also benefit from this therapy.

treatment with pegfilgrastim as primary prophylaxis for febrile neutropenia could improve outcomes by enabling more aggressive treatment Consumer comments · PSD
treatment efficacyunmet needaccess to therapyclinical outcomes

Similar precedents

By decision profile

Regulatory · TGA

Label narrower than PBS population — PBAC restricts to curative-intent chemotherapy and specific febrile neutropenia risk thresholds; TGA label covers all post-chemotherapy neutropenia.