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IdelalisibZYDELIG (100 mg and 150 mg idelalisib) tablets

Recommended HaematologyAuthority RequiredLater-line line 💬 consumer voice

Refractory follicular B-cell non-Hodgkin's lymphoma in patients refractory to both rituximab and an alkylating agent, as monotherapy.

8
Submissions
6 resub
2015–16
On the record
$45k–75k
ICER range
2 sourced ICERs · 2016
Redacted
Cost basis
risk sharing

Decisions on record

9 decisions
  • Meeting Aug 2016 Recommended Chronic lymphocytic leukaemia and small lymphocytic lymphoma no PSD
  • Meeting Jul 2016 Recommended Chronic lymphocytic leukaemia and small lymphocytic lymphoma
  • Meeting Jul 2016 Recommended Follicular Lymphoma
  • Meeting Mar 2016 Deferred Follicular lymphoma
  • Meeting Mar 2016 Deferred Chronic lymphocytic leukaemia (CLL) and small lymphocytic lymphoma (SLL).
  • Meeting Nov 2015 Deferred Follicular lymphoma
  • Meeting Nov 2015 Deferred Chronic lymphocytic leukaemia
  • Meeting Mar 2015 Not recommended chronic lymphocytic leukaemia
1 earlier decision
  • Mar 2015 Not recommended Non-Hodgkin's lymphoma

Access path

8 submissions · public record
  1. TGA registered · ZYDELIG (100 mg and 150 mg idelalisib) tablets

    TGA label narrower than the PBS population

  2. Mar 2015
    Not recommended

    Comparator changed: rituximab monotherapy and/or best supportive care (for patients truly…

  3. Mar 2015
    Not recommended

    Comparator changed: rituximab monotherapy and/or best supportive care (for patients truly…

  4. Nov 2015
    Not recommended

    Immature overall survival data, concerns regarding RPSFT methodology and confidence intervals, uncertainty in OS hazard…

  5. Nov 2015
    Deferred

    Evidence: Single-arm → RCT

  6. Mar 2016
    Deferred

    Comparator changed: best supportive care → rituximab monotherapy (best supportive care)

  7. Mar 2016
    Deferred

    Comparator changed: best supportive care → rituximab monotherapy (best supportive care)

  8. Jul 2016
    Recommended · restricted
  9. Jul 2016
    Recommended · restricted
  10. PBS listing · Authority Required
RecommendedDeferredNot recommended

From the public summary

Verbatim · PSD text · may span indications
PBAC outcome
5.1 The PBAC recommended the Authority Required listing of idelalisib in combination with rituximab for the treatment of relapsed or refractory chronic lymphocytic leukaemia (CLL) or small lymphocytic leukaemia (SLL). The PBAC was satisfied that idelalisib provides, for some patients, a significant improvement in efficacy over best supportive care.PSD · Jul 2016
5.2 The PBAC acknowledged that the safety signals observed in the Phase 3 trials, resulting in the March 2016 submission deferral, were not identified in a re-analysis of the clinical trials that have been considered by the PBAC in the support of the proposed listing.PSD · Jul 2016
Economic analysis
6.31 The resubmission presented a cost-utility analysis, based on the results of Trial 312-0116. A comparison between the model presented in the resubmission and the previous submission is summarised in Table 7.PSD · Nov 2015
1 Latimer N. Survival analysis for economic evaluations alongside clinical trials – extrapolation with patient-level data: inconsistencies, limitations and a practical guide. Med Decis Making. 2013 Aug;33(6):743-54 13PSD · Nov 2015
Clinical claim
6.23 The resubmission described idelalisib plus rituximab as having superior comparative 11PSD · Nov 2015
6.24 This superior comparative effectiveness claim might be reasonably supported:  the PBAC considered that placebo plus rituximab might be a reasonable proxy for best supportive care in this patient group for overall survival (Item 7.8, March 2015 PBAC)  idelalisib plus rituximab showed superior progression free survival and overall survival benefits compared to placebo plus rituximab, using the ITT analysis.PSD · Nov 2015
Consumer comments
4.2 The PBAC noted and welcomed the input from an organisation (1) via the Consumer Comments facility on the PBS website. The comment reiterated the lack of treatment options for patients with follicular lymphoma and highlighted the importance of providing another therapeutic option for these patients. 2PSD · Jul 2016
Financial management – risk sharing
6.52 The resubmission proposed a '''''''% discount on the dispensed price for maximum quantity (DPMQ) price. 19PSD · Nov 2015

Cost-effectiveness

2 sourced ICERs · 2016

ICER value not stated in public summary document; document notes PBAC 'maintained that the ICER remained high' but no numeric value provided.

The PBAC maintained that the ICER remained high but considered this acceptable for this patient population for whom there are few treatment options. PBAC · 2016
ICER uncertainICER / price too highEconomic model disputedPrice cut / RSA neededNo head-to-head trialIndirect comparisonCost-effectiveness accepted ×2

Decision context

PopulationPatients with follicular B-cell non-Hodgkin's lymphoma that is refractory to both rituximab and an alkylating agent, as monotherapy.

Risk sharingRisk sharing arrangement with financial cap recommended; cap based on utilisation estimates in March 2016 submission; utilisation to be reviewed 3 years after listing.

Submission history

8 entries
DecidedOutcomeComparatorICEREvidence
Jul 2016 Recommended · restricted best supportive care RCT · OS
Jul 2016 Recommended · restricted best supportive care Single-arm · PFS
Mar 2016 Deferred rituximab monotherapy (best supportive care) $45k–75k RCT · OS
Mar 2016 Deferred best supportive care $45k–75k RCT · PFS
Nov 2015 Not recommended best supportive care RCT · PFS
Nov 2015 Deferred best supportive care Single-arm · PFS
Mar 2015 Not recommended rituximab monotherapy and/or best supportive care (for patients truly unable to tolerate chemo-immunotherapy); chemo-imm RCT · PFS
Mar 2015 Not recommended best supportive care Single-arm · ORR

Codependent tests

MSAC
ServiceBiomarkerMSAC outcomeYear
Genome-wide microarray testing for multiple myeloma and chronic lymphocytic leukaemia del(17p) and other chromosomal abnormalities supported 2019
17p deletion testing by FISH for CLL/SLL 17p deletion (del(17p)) supported 2019
17p deletion testing (FISH) for CLL/SLL 17p deletion (del(17p)) supported 2020

Consumer voice

Jul 2016

One consumer organisation highlighted the lack of treatment options for patients with follicular lymphoma and emphasised the importance of providing another therapeutic option for these patients.

The comment reiterated the lack of treatment options for patients with follicular lymphoma and highlighted the importance of providing another therapeutic option for these patients. Consumer comments · PSD
unmet needaccess barrierstreatment options

Similar precedents

By decision profile

Regulatory · TGA

Label narrower than PBS population — PBAC restricts to rituximab AND alkylating agent refractoriness; TGA label requires only two prior systemic therapies without specifying drug classes.