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Patiromer

Recommended EndocrinologyAuthority RequiredFirst-line line 💬 consumer voice

Initial treatment of adult patients with chronic kidney disease (CKD) Stage 3-4, with chronic hyperkalaemia (at least two episodes of serum potassium 6.0 mmol/L or higher in the previous 12 months), who are receiving at least one renin angiotensin aldosterone system inhibitor (RAASi) medicine or are indicated for a RAASi medicine but are unable to tolerate it due to prior occurrence of hyperkalaemia.

4
Submissions
3 resub
2019–23
On the record
ICER range
Cost-min
Cost basis
risk sharing

Decisions on record

3 decisions
  • Meeting Mar 2023 Recommended Hyperkalaemia; chronic hyperkalaemia in CKD Stage 3-4 patients
  • Meeting Nov 2022 Not recommended Chronic hyperkalaemia in chronic kidney disease Stage 3 or 4
  • Meeting Nov 2020 Not recommended Patiromer is indicated for the treatment of hyperkalaemia in adults.

Access path

4 submissions · public record
  1. Nov 2019
    Not recommended

    unclear clinical criteria and eligibility definition for hyperkalaemia requiring pharmacological intervention…

  2. Nov 2020
    Not recommended

    Comparator changed: placebo → standard care (low K+ diet and RAASi therapy)

  3. Nov 2022
    Not recommended

    Comparator changed: standard care (low K+ diet and RAASi therapy) → standard care (RAASi…

  4. ↻ resubmitted
    Mar 2023
    Recommended

    Comparator changed: standard care (RAASi reduction or withdrawal with or without dietary…

  5. PBS listing · Authority Required
RecommendedDeferredNot recommended

From the public summary

Verbatim · PSD text · may span indications
PBAC outcome
5.1 The PBAC recommended the listing of patiromer for the treatment of adult patients with chronic kidney disease (CKD) Stage 3-4, with chronic hyperkalaemia (at least two episodes of serum potassium ≥ 6.0 mmol/L in the previous 12 months), who are receiving at least one renin angiotensin aldosterone system inhibitor (RAASi) or are indicated for a RAASi but are unable to tolerate it due to prior occurrence of hyperkalaemia.PSD · Mar 2023
5.2 The PBAC acknowledged the consumer comments relating to patiromer which described the benefits of treatment and highlighted the need for safe, effective, and palatable therapies in this setting. The comments also highlighted the issues with the existing therapies such as gastrointestinal adverse events and lack of palatability.PSD · Mar 2023
Economic analysis
4.5 In November 2022, the PBAC considered ‘it would be appropriate for any future resubmission to be based solely on the cost minimisation approach versus SPS/CPS resins presented by the evaluators in chronic hyperkalaemia patients (per Table 16, which resulted in a cost per pack of patiromer of $ in the submission and $ in the Pre- Sub-Committee Response (PSCR) (as the gastrointestinal adverse event costs were removed)).PSD · Mar 2023
4.6 The resubmission based the proposed price of patiromer solely on a cost minimisation approach (CMA), consistent with the PBAC’s previous advice. However, compared with the CMA presented in the November 2022 submission, the key difference was that the average daily dose of SPS and CPS resins was based on the dose recommended in the Product Information of 15 g three to four times a day, with the resubmission applying a daily dose of 45 g (this had been …PSD · Mar 2023
Clinical claim
4.3 The resubmission described patiromer as non-inferior in terms of effectiveness and safety compared to SPS/CPS resins, noting patiromer is associated with fewer gastrointestinal adverse events (AEs) and improved tolerability. This was consistent with the PBAC’s previous advice in November 2022, in which the PBAC considered that patiromer was:PSD · Mar 2023
• non-inferior compared to SPS/CPS resins in terms of reducing potassium levels (paragraph 6.48, patiromer PSD, November 2022 PBAC Meeting).PSD · Mar 2023
Consumer comments
4.2 The PBAC noted and welcomed the input from health care professionals (10) via the Consumer Comments facility on the PBS website. The comments described the benefits of treatment with patiromer including the improved tolerability and palatability compared to currently available therapies.PSD · Mar 2023
Financial management – risk sharing
4.24 The resubmission did not propose an RSA. The PBAC previously advised that a resubmission should include ‘an RSA based on the revised financial impact estimates with expenditure caps, beyond which a rebate of % would be applied’ (paragraph 7.14, patiromer PSD, November 2022 PBAC Meeting). For more detail on PBAC’s view, see section 5 PBAC outcome.PSD · Mar 2023

Cost-effectiveness

Cost-minimisation analysis; no ICER calculated. PBAC advised that cost-utility analysis was unreliable and a cost-minimisation approach versus SPS/CPS resins was appropriate.

The PBAC considered that the claim of superior comparative effectiveness compared to placebo was unclear. PBAC · 2019
ICER uncertain ×2Economic model disputed

Decision context

PopulationAdults with chronic kidney disease Stage 3-4, chronic hyperkalaemia (at least 2 episodes of serum potassium ≥6.0 mmol/L in previous 12 months), receiving or indicated for RAASi but unable to tolerate due to prior hyperkalaemia.

Risk sharingRisk sharing arrangement presented based on revised financial estimates with expenditure caps beyond which a rebate of % was applied.

Submission history

4 entries
DecidedOutcomeComparatorICEREvidence
Mar 2023 Recommended sodium polystyrene sulfonate (SPS) and calcium polystyrene sulfonate (CPS) Cost-minimisation · Cost-minimisation
Nov 2022 Not recommended standard care (RAASi reduction or withdrawal with or without dietary modification) and sodium polystyrene sulfonate (SPS RCT · Serum potassium reduction
Nov 2020 Not recommended standard care (low K+ diet and RAASi therapy) RCT · Other
Nov 2019 Not recommended placebo RCT · Other

Clinical evidence

Trials cited in the PSDs · ClinicalTrials.gov
TrialPhaseNPrimary outcomeStatus
OPAL-HK Ph 3 243 Change in Serum Potassium From Part A Baseline to Part A Week 4 completed
AMETHYST-DN Ph 2 324 Least Squares Mean Change in Serum Potassium From Baseline to Week 4 or Time of First Titr… completed
TOURMALINE Ph 4 114 Percentage of Subjects With Serum Potassium in the Target Range (3.8 - 5.0 mEq/L) at Eithe… completed
DIAMOND Ph 3 1,195 Changes in Serum K+ Levels From Baseline completed
PEARL-HF Ph 2 120 Change From Baseline in Serum Potassium to the End of the 28-day Treatment Period. completed
AMBER Ph 2 295 Number of Participants Remaining on Spironolactone at Week 12 completed

Consumer voice

Mar 2023

Healthcare professionals provided input via the PBS website describing the benefits of patiromer treatment, particularly its improved tolerability and palatability compared to currently available therapies including SPS/CPS resins.

The comments described the benefits of treatment with patiromer including the improved tolerability and palatability compared to currently available therapies. Consumer comments · PSD
tolerabilitypalatabilityside effectstreatment burden

Similar precedents

By decision profile

Regulatory · TGA

Label narrower than PBS population — PBAC restricts to CKD Stage 3-4, chronic hyperkalaemia with specific potassium thresholds and RAASi indication/intolerance; TGA label is all adults with hyperkalaemia.