Amino acid formula with vitamins and minerals, low phenylalanine and supplemented with docosahexaenoic acid and arachidonic acid

PBAC's latest decision on Amino acid formula with vitamins and minerals, low phenylalanine and supplemented with docosahexaenoic acid and arachidonic acid: Recommended (2019). Considered for Dietary management of phenylketonuria (PKU) in older infants and young children.

Eligible population

Infants and young children aged from weaning-age to 5 years with phenylketonuria (PKU) diagnosed by newborn screening.

Therapy area

Metabolic

Line of therapy

Not applicable

Evidence base

Single-arm

Primary endpoint

Acceptability and tolerance

Pivotal trial size

19 patients

Comparator

PKU Anamix First Spoon

Economic model

Cost-minimisation

ICER note

Cost-minimisation analysis; no ICER calculated by design.

Submission history

• Mar 2017: Recommended with restriction · Restricted
• Jul 2019: Recommended · Restricted

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