Disease index

primary hyperoxaluria type 1

Rare disease · 2025–2025

1decision
1medicine
1carried consumer input
6individual submissions

Every decision

MedicineMeetingOutcomeConsumer input
lumasiran Primary hyperoxaluria type 1 (PH1) in patients with elevated urinary oxalate levels or clinical symptoms indicative of hyperoxaluria, as an addition to best… Mar 2025 Recommended with restriction 6 individuals

Conditions are classified by a language model from the indication text of each submission, so an individual label here can be wrong. Consumer input is read from the document's own consumer comments section: 1 of 1 decisions since 2014 carried some. Silence means no comment reached the committee through that facility, not that nobody was affected. More on how this was built.