Disease index

PNH

Haematology · 2010–2024

2decisions
2medicines
1carried consumer input
0individual submissions

Every decision

MedicineMeetingOutcomeConsumer input
iptacopan Treatment of adults with paroxysmal nocturnal haemoglobinuria (PNH) who have inadequate clinical response to C5 inhibitor treatment. Jul 2024 Recommended input received
eculizumab treatment of paroxysmal nocturnal haemoglobinuria (PNH) to reduce haemolysis Jul 2010 Recommended with restriction no section in document

Conditions are classified by a language model from the indication text of each submission, so an individual label here can be wrong. Consumer input is read from the document's own consumer comments section: 1 of 1 decisions since 2014 carried some. Silence means no comment reached the committee through that facility, not that nobody was affected. More on how this was built.