phenylketonuria (PKU)
Metabolic · 2022–2022
1decision
1medicine
1carried consumer input
145individual submissions
Every decision
| Medicine | Meeting | Outcome | Consumer input |
|---|---|---|---|
| pegvaliase Hyperphenylalaninemia (HPA) due to phenylketonuria (PKU) in patients aged 16 years and over who are not responsive to sapropterin. | Jul 2022 | Not recommended | 145 individuals Metabolic Dietary Disorders Association · PKU Association · Rare Voices Australia |
Who spoke
Metabolic Dietary Disorders Association · PKU Association · Rare Voices Australia
Conditions are classified by a language model from the indication text of each submission, so an individual label here can be wrong. Consumer input is read from the document's own consumer comments section: 1 of 1 decisions since 2014 carried some. Silence means no comment reached the committee through that facility, not that nobody was affected. More on how this was built.