phenylketonuria (BH4-deficient)
Metabolic · 2012–2012
Every decision here pre-dates the consumer comments facility, so no input would be recorded either way.
Every decision
| Medicine | Meeting | Outcome | Consumer input |
|---|---|---|---|
| sapropterin Treatment of hyperphenylalaninaemia (HPA) in patients demonstrated to have tetrahydrobiopterin (BH4) deficiency. | Jul 2012 | Noted | no section in document |
What the PBS pays
$17M in government benefit over 2024–25, across 2,436 services.
This is spend on the medicines considered for this condition, not spend on the disease. A medicine used for several conditions is counted in full under each, so figures across conditions add to more than national PBS expenditure.
| Medicine | Government benefit |
|---|---|
| sapropterin | $17.3M |
Conditions are classified by a language model from the indication text of each submission, so an individual label here can be wrong. Consumer input is read from the document's own consumer comments section: 0 of 0 decisions since 2014 carried some. Silence means no comment reached the committee through that facility, not that nobody was affected. More on how this was built.