Disease index

mucopolysaccharidosis type VI

Rare disease · 2007–2007

1decision
1medicine
0carried consumer input
0individual submissions

Every decision here pre-dates the consumer comments facility, so no input would be recorded either way.

Every decision

MedicineMeetingOutcomeConsumer input
galsulfase Treatment of mucopolysaccharidosis type VI (MPS VI), a rare inherited lysosomal storage disorder characterized by deficiency of the enzyme arylsulfatase B. Jul 2007 Recommended no section in document

Conditions are classified by a language model from the indication text of each submission, so an individual label here can be wrong. Consumer input is read from the document's own consumer comments section: 0 of 0 decisions since 2014 carried some. Silence means no comment reached the committee through that facility, not that nobody was affected. More on how this was built.