mucopolysaccharidosis type IVA
Rare disease · 2016–2016
1decision
1medicine
1carried consumer input
444individual submissions
Every decision
| Medicine | Meeting | Outcome | Consumer input |
|---|---|---|---|
| elosulfase alfa Treatment of patients with mucopolysaccharidosis (MPS) IVA (Morquio A Syndrome), a rare inherited lysosomal storage disorder characterised by progressive… | Mar 2016 | Not recommended | 444 individuals Related Diseases Society Australia · MPS Australia |
Who spoke
Related Diseases Society Australia · MPS Australia
Conditions are classified by a language model from the indication text of each submission, so an individual label here can be wrong. Consumer input is read from the document's own consumer comments section: 1 of 1 decisions since 2014 carried some. Silence means no comment reached the committee through that facility, not that nobody was affected. More on how this was built.