Disease index

maternal phenylketonuria

Metabolic · 2020–2020

1decision
1medicine
1carried consumer input
35individual submissions

Every decision

MedicineMeetingOutcomeConsumer input
sapropterin Treatment of hyperphenylalaninaemia (HPA) due to phenylketonuria (PKU) in pregnant women or women actively planning to become pregnant, in combination with a… Dec 2020 Recommended with restriction 35 individuals

Conditions are classified by a language model from the indication text of each submission, so an individual label here can be wrong. Consumer input is read from the document's own consumer comments section: 1 of 1 decisions since 2014 carried some. Silence means no comment reached the committee through that facility, not that nobody was affected. More on how this was built.