Disease index

lysosomal acid lipase deficiency

Metabolic · 2022–2022

1decision
1medicine
1carried consumer input
0individual submissions

Every decision

MedicineMeetingOutcomeConsumer input
sebelipase alfa Infantile onset lysosomal acid lipase deficiency (LAL-D), also known as rapidly progressive LAL-D or Wolman disease. Mar 2022 Not recommended input received

Conditions are classified by a language model from the indication text of each submission, so an individual label here can be wrong. Consumer input is read from the document's own consumer comments section: 1 of 1 decisions since 2014 carried some. Silence means no comment reached the committee through that facility, not that nobody was affected. More on how this was built.