hyperphenylalaninaemia
Metabolic · 2012–2019
2decisions
1medicine
0carried consumer input
0individual submissions
No submission for this condition has carried consumer input, including the one made since the comments facility came into use.
Every decision
| Medicine | Meeting | Outcome | Consumer input |
|---|---|---|---|
| sapropterin Hyperphenylalaninaemia (HPA) due to tetrahydrobiopterin (BH4) deficiency and HPA due to phenylketonuria (PKU). The submission requested listing of 100 mg and… | Jul 2019 | Recommended with restriction | none received |
| sapropterin Treatment of hyperphenylalaninaemia (HPA) in patients demonstrated to have tetrahydrobiopterin (BH4) deficiency. | Jul 2012 | Noted | no section in document |
Conditions are classified by a language model from the indication text of each submission, so an individual label here can be wrong. Consumer input is read from the document's own consumer comments section: 0 of 1 decisions since 2014 carried some. Silence means no comment reached the committee through that facility, not that nobody was affected. More on how this was built.